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Rare Disease Day 2018

This year Rare Disease day will fall on Wednesday the 28th of February. The main objective of Rare Disease Day is to raise awareness amongst the general public and decision-makers about rare diseases and their impact on patients’ lives.The campaign targets primarily the general public and also seeks to raise awareness amongst policy makers, public authorities, industry representatives, researchers, health professionals and anyone who has a genuine interest in rare diseases.

Pompe Treatment Trials

Amicus released at the 22nd International Congress of the World Muscle Society in France on the 4th October 2017 details of their Pompe treatment trials for ATB200/AT2221.

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